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Exhibitors - WORLDSymposium 2025 - (formerly Lysosomal Disease Research Symposium)
(35)

Exhibitor Name Contact Booth No Phone Email
Amicus Therapeutics verified
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ARCHIMEDlife verified
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Astellas Gene Therapies verified
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Azafaros B.V. verified
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BioMarin Pharmaceutical Inc. verified
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Chiesi Global Rare Diseases verified
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Denali Therapeutics verified
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Gaucher Community Alliance verified
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Global Genes verified
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Greenwood Genetic Center verified
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Immusoft Corporation verified
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Inozyme verified
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International Niemann Pick Disease Alliance verified
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International Sanfilippo Syndrome Alliance verified
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JCR Pharmaceuticals Co., Ltd. verified
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Living in the Light of Rare Diseases verified
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Lysosomal & Rare Disorders Research & Treatment Center verified
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Mirum Pharmaceuticals verified
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MLD Foundation verified
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Multicare Pharma verified
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National MPS Society verified
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National Organization for Rare Disorders verified
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National Tay-Sachs & Allied Diseases Assoc. verified
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Orchard Therapeutics verified
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Passage Bio verified
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Pearson Clinical Assessment verified
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Pompe Support Network verified
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QPS LLC verified
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Sanofi verified
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Takeda Pharmaceutical Company Limited verified
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The Assistance Fund verified
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Ultragenyx verified
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United MSD Foundation verified
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Worldwide Clinical Trials verified
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Zevra Therapeutics verified
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